Quantitative Antisense Screening and Optimization for Exon 51 Skipping in Duchenne Muscular Dystrophy

Echigoya, Yusuke; Lim, Kenji Rowel Q.; Trieu, Nhu; Bao, Bo; Miskew Nichols, Bailey; Vila, Maria Candida; Novak, James S.; Hara, Yuko; Lee, Joshua; Touznik, Aleksander; Mamchaoui, Kamel; Aoki, Yoshitsugu; Takeda, Shin’ichi; Nagaraju, Kanneboyina; Mouly, Vincent; Maruyama, Rika; Duddy, William; Yokota, Toshifumi

doi:10.1016/j.ymthe.2017.07.014

Title: Quantitative Antisense Screening and Optimization for Exon 51 Skipping in Duchenne Muscular Dystrophy

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Authors:: Echigoya, Yusuke; Lim, Kenji Rowel Q.; Trieu, Nhu; Bao, Bo; Miskew Nichols, Bailey; Vila, Maria Candida; Novak, James S.; Hara, Yuko; Lee, Joshua; Touznik, Aleksander; Mamchaoui, Kamel; Aoki, Yoshitsugu; Takeda, Shin’ichi; Nagaraju, Kanneboyina; Mouly, Vincent; Maruyama, Rika; Duddy, William; Yokota, Toshifumi

Publication Date:: Wed Nov 01 00:00:00 EDT 2017

Sponsoring Org.:: USDOE

OSTI Identifier:: 1481833

Grant/Contract Number:: W81XWH-05-1-0616; W81XWH-11-1-0782

Resource Type:: Published Article

Journal Name:: Molecular Therapy

Additional Journal Information:: Journal Name: Molecular Therapy Journal Volume: 25 Journal Issue: 11; Journal ID: ISSN 1525-0016

Publisher:: Elsevier

Country of Publication:: Country unknown/Code not available

Language:: English

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                    Echigoya, Yusuke, Lim, Kenji Rowel Q., Trieu, Nhu, Bao, Bo, Miskew Nichols, Bailey, Vila, Maria Candida, Novak, James S., Hara, Yuko, Lee, Joshua, Touznik, Aleksander, Mamchaoui, Kamel, Aoki, Yoshitsugu, Takeda, Shin’ichi, Nagaraju, Kanneboyina, Mouly, Vincent, Maruyama, Rika, Duddy, William, and Yokota, Toshifumi. Quantitative Antisense Screening and Optimization for Exon 51 Skipping in Duchenne Muscular Dystrophy.  Country unknown/Code not available: N. p., 2017. 
Web.  doi:10.1016/j.ymthe.2017.07.014.

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                    Echigoya, Yusuke, Lim, Kenji Rowel Q., Trieu, Nhu, Bao, Bo, Miskew Nichols, Bailey, Vila, Maria Candida, Novak, James S., Hara, Yuko, Lee, Joshua, Touznik, Aleksander, Mamchaoui, Kamel, Aoki, Yoshitsugu, Takeda, Shin’ichi, Nagaraju, Kanneboyina, Mouly, Vincent, Maruyama, Rika, Duddy, William, & Yokota, Toshifumi. Quantitative Antisense Screening and Optimization for Exon 51 Skipping in Duchenne Muscular Dystrophy.  Country unknown/Code not available.  https://doi.org/10.1016/j.ymthe.2017.07.014

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                    Echigoya, Yusuke, Lim, Kenji Rowel Q., Trieu, Nhu, Bao, Bo, Miskew Nichols, Bailey, Vila, Maria Candida, Novak, James S., Hara, Yuko, Lee, Joshua, Touznik, Aleksander, Mamchaoui, Kamel, Aoki, Yoshitsugu, Takeda, Shin’ichi, Nagaraju, Kanneboyina, Mouly, Vincent, Maruyama, Rika, Duddy, William, and Yokota, Toshifumi. Wed .  
"Quantitative Antisense Screening and Optimization for Exon 51 Skipping in Duchenne Muscular Dystrophy".  Country unknown/Code not available.  https://doi.org/10.1016/j.ymthe.2017.07.014.

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@article{osti_1481833,

  title        = {Quantitative Antisense Screening and Optimization for Exon 51 Skipping in Duchenne Muscular Dystrophy},

  author       = {Echigoya, Yusuke and Lim, Kenji Rowel Q. and Trieu, Nhu and Bao, Bo and Miskew Nichols, Bailey and Vila, Maria Candida and Novak, James S. and Hara, Yuko and Lee, Joshua and Touznik, Aleksander and Mamchaoui, Kamel and Aoki, Yoshitsugu and Takeda, Shin’ichi and Nagaraju, Kanneboyina and Mouly, Vincent and Maruyama, Rika and Duddy, William and Yokota, Toshifumi},

  abstractNote = {},

  doi          = {10.1016/j.ymthe.2017.07.014},

  journal      = {Molecular Therapy},

  number       = 11,

  volume       = 25,

  place        = {Country unknown/Code not available},

  year         = {Wed Nov 01 00:00:00 EDT 2017},

  month        = {Wed Nov 01 00:00:00 EDT 2017}

}

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